Cellular & Molecular Medicine: Open access

Gene therapy is a technique of therapeutic delivery of nucleic acid polymers as a drug into the cell of patient’s to treat disease. The polymer are targeted to possibly correct gene mutation. Gene therapy is an experimental technique that uses genes to treat or prevent disease. In the future, this technique may allow doctors to treat a disorder by inserting a gene into a patient’s cells instead of using drugs or surgery. Although gene therapy is a promising treatment option for a number of diseases (including inherited disorders, some types of cancer, and certain viral infections), the technique remains risky and is still under study to make sure that it will be safe and effective. Gene therapy is currently only being tested for the treatment of diseases that have no other cures.